ABCDE
1
Rare DiseasePrimary Nonprofit OrganizationWebsiteCountryNotes
2
AcromegalyAcromegaly Community
https://www.acromegalycommunity.org
USA
3
ALSALS Associationhttps://www.als.orgUSA
4
Angelman SyndromeAngelman Syndrome Foundationhttps://www.angelman.orgUSA
5
Batten Disease
Batten Disease Support & Research Association
https://bdsra.orgUSA
6
Cystic FibrosisCystic Fibrosis Foundationhttps://www.cff.orgUSA
7
Duchenne Muscular DystrophyParent Project Muscular Dystrophyhttps://www.parentprojectmd.orgUSA
8
Ehlers-Danlos SyndromesThe Ehlers-Danlos Societyhttps://www.ehlers-danlos.comUSA
9
Fabry DiseaseNational Fabry Disease Foundationhttps://www.fabrydisease.orgUSA
10
Fibrous Dysplasia / McCune-Albright Syndrome
FD/MAS Alliancehttps://fdmasalliance.orgUSA
11
Fragile X SyndromeFRAXA Research Foundationhttps://www.fraxa.orgUSA
12
Friedreich's AtaxiaFARAhttps://www.curefa.orgUSA
13
Gaucher DiseaseNational Gaucher Foundationhttps://www.gaucherdisease.orgUSA
14
HemophiliaNational Bleeding Disorders Foundationhttps://www.bleeding.orgUSA
15
Hereditary AngioedemaUS Hereditary Angioedema Associationhttps://www.haea.orgUSA
16
Huntington's DiseaseHuntington's Disease Society of Americahttps://hdsa.orgUSA
17
Idiopathic Pulmonary FibrosisPulmonary Fibrosis Foundationhttps://www.pulmonaryfibrosis.orgUSA
18
Marfan SyndromeThe Marfan Foundationhttps://marfan.orgUSA
19
NeurofibromatosisChildren's Tumor Foundationhttps://www.ctf.orgUSA
20
Pompe DiseaseAcid Maltase Deficiency Associationhttps://www.amda-pompe.orgUSA
21
Prader-Willi SyndromePrader-Willi Syndrome Association USAhttps://www.pwsausa.orgUSA
22
Rett SyndromeInternational Rett Syndrome Foundationhttps://www.rettsyndrome.orgUSA
23
Sickle Cell DiseaseSickle Cell Disease Association of Americahttps://www.sicklecelldisease.orgUSA
24
Spinal Muscular AtrophyCure SMAhttps://www.curesma.orgUSA
25
Tuberous Sclerosis ComplexTSC Alliancehttps://www.tscalliance.orgUSA
26
Xeroderma PigmentosumXP Family Support Grouphttps://xpfamilysupport.orgUSA
27
28
29
30
31
32
33
34
35
36
37
38
39
40
41
42
43
44
45
46
47
48
49
50
51
52
53
54
55
56
57
58
59
60
61
62
63
64
65
66
67
68
69
70
71
72
73
74
75
76
77
78
79
80
81
82
83
84
85
86
87
88
89
90
91
92
93
94
95
96
97
98
99
100