1 of 1

2024 Policy Actions

  • Engaged with Congressional Rare Disease Champions and Stakeholders including:
    • Direct Hill advocacy and with Staff for key offices, including Rep. Matsui (D-CA) and Rep. Bilirakis (R-FL), Chairs of the Rare Disease Caucus, Rep. Judy Chu (D-CA), Chair of the Congressional Asian Pacific American Caucus, and Sen. Cory Booker (D-NJ)
    • Presented awards to Sen. Booker and Sen. Scott for their leadership on health priorities
    • Authored and popularized advocacy letters on: Accessible Air Travel, and Rare Pediatric Disease PRV
    • Advised on draft legislation, including the Externally-Led Scientific-Focused Drug Development (EL-SFDD) meeting at FDA
  • Engaged with the Biden Administrative and Agencies (e.g., White House, CMS, FDA, HHS)
    • Met with the White House on leveraging RDDC to advance Women’s Health Research and Innovation
    • Submitted comments, on the record, on important regulations, including: FDA Diversity Action Plan Guidance, and DOT Accessible Air Travel
  • Supported and Collaborated with Rare Disease Advocates
    • Signed on to letters, including on rare kidney disease in the AAPI
    • Presented at coalition meetings on policy development around key legislation
  • Collaborating with Rep. Marilyn Strickland’s Office on Comprehensive Rare Disease Research legislation for introduction in the 119th Congress