The effects of caffeine use in NICU on the neurodevelopmental outcome of premature infants: A
prospective review
Lauren Phung1, Rawad Obeid, MD2
1Oakland University William Beaumont School of Medicine, 2Dept. Of Pediatric Neurology, Corewell Health East
- Prematurity remains a major cause of neonatal morbidity as the developing brain is vulnerable to intermittent hypoxia and inflammation.
- Caffeine citrate (CC) is a cornerstone therapy in the NICU for apnea of prematurity, with neuroprotective effects through antioxidation and anti inflammation.1,2
Figure 1: Molecular mechanisms of Caffeine
(Created with BioRender.com)
- Early administration within 48 hours after birth appears to mitigate neurodevelopmental impairments in preclinical and clinical studies, though additional prospective studies of the long-term neuroprotective effects of CC are needed.3
- High daily average dose caffeine was associated with better motor, language, and cognitive performance than low-dose caffeine in multivariable analyses adjusted for gestational age and respiratory disease.4
- Evaluate the consistency the protocol of CC administration at NICU Corewell Health East NICU between the years of 2020 and 2024.
- Evaluate the cumulative dose of CC given in NICU on the neurodevelopmental outcomes of preterm infants measured at follow-up visits.
- The cumulative dose of caffeine is calculated as the sum of the initiation dose and the product of the maintenance dose and the number of days on maintenance.
- Alberta Infant Motor Score (AIMS), Peabody scores, and Bayley III scores are also collected at follow-up visits. Rating for the referenced scores is determined as follows:
- AIMS score < 10th percentile is abnormal
- Peabody Grasp and Visual: ∆ Peabody score in months and corrected age in months is within 2 STDs (1 STD = 1 month), neurodevelopment is marked as consistent.
- Bayley III score < 85 is abnormal
Results
- The following variables were collected: demographics, birth weight, neonatal comorbidities, Apgar scores, evidence of caffeine administration, and duration of mechanical ventilation.
References
- Kolahdouzan M, Hamadeh MJ. The neuroprotective effects of caffeine in neurodegenerative diseases. CNS Neurosci Ther. 2017;23(4):272-290. doi:10.1111/cns.12684
- Kong H, Jones PP, Koop A, Zhang L, Duff HJ, Chen SR. Caffeine induces Ca2+ release by reducing the threshold for luminal Ca2+ activation of the ryanodine receptor. Biochem J. 2008;414(3):441-452. doi:10.1042/BJ20080489
- Helwich E, Rutkowska M, Bokiniec R, Gulczyńska E, Hożejowski R. Intraventricular hemorrhage in premature infants with Respiratory Distress Syndrome treated with surfactant: incidence and risk factors in the prospective cohort study. Dev Period Med. 2017;21(4):328-335.
doi:10.34763/devperiodmed.20172104.328335
- Ostrem BEL, Odell E, Grelli KN, et al. Cumulative caffeine exposure predicts neurodevelopmental outcomes in premature infants. Pediatr Res. Published online September 20, 2025. doi:10.1038/s41390-025-04387-1
- Clinical comorbidities including PVL, SGA, PDA, BPD, and NEC, as well as low birth weight and low Apgar score are most significantly associated with a higher likelihood of reduced AIMS scores at short-term follow-up, consistent with current literature.
- Higher cumulative doses of caffeine citrate were not significantly associated with improvements in short- or long-term neurodevelopmental scores. This lack of significance may stem from unmeasured confounding factors or the extreme ranges of cumulative caffeine dosing observed within the current sample.
- Subsequent studies will evaluate the impact of average daily caffeine dosage using an expanded sample size and multivariate adjustments to minimize multicollinearity among clinical characteristics.
Discussion
- Within the Corewell Health system, approximately 99.9% of preterm infants born at <32 weeks’ gestational age receive caffeine citrate within the first 24 hours of life.
Table 1: Univariate analysis of the effects of clinical characteristics of the cohort and cumulative dose of caffeine on the neurodevelopmental outcomes of
<32 GAS weeks preterm infants.
(*p-value < 0.05; OR of impairment for categorical variables; OR of no impairment for continuous variable; Firth's correction with the logistic regression
models was used to account for the smaller sample size of the Bayley III scores)
CC: Caffeine citrate
SGA: Small gestational age
PVL: periventricular leukomalacia BPD: Bronchopulmonary dysplasia NEC: necrotizing enterocolitis
DART: Dexamethasone: A Randomized Trial
OR: Odd ratio
NICU: Neonatal intensive care unit